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Gene therapy for cystic fibrosis: recent progress and current aims

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Review - Gene therapy for CF 2015.docxAccepted version80.67 kBMicrosoft WordView/Open
Figures.pptAccepted version334.5 kBMicrosoft PowerpointView/Open
Title: Gene therapy for cystic fibrosis: recent progress and current aims
Authors: Paul-Smith, MC
Bell, RV
Alton, WE
Alton, EWFW
Griesenbach, U
Item Type: Journal Article
Issue Date: 6-May-2016
Date of Acceptance: 18-Apr-2016
URI: http://hdl.handle.net/10044/1/32253
DOI: https://dx.doi.org/10.1080/21678707.2016.1180974
ISSN: 2167-8707
Publisher: Taylor and Francis
Start Page: 649
End Page: 658
Journal / Book Title: Expert Opinion on Orphan Drugs
Volume: 4
Issue: 6
Copyright Statement: © 2016 Taylor & Francis. This is an Author's Accepted Manuscript of an article published in Expert Opinion on Orphan Drugs, available online at: http://dx.doi.org/10.1080/21678707.2016.1180974
Sponsor/Funder: Medical Research Council (MRC)
Cystic Fibrosis Trust
Funder's Grant Number: MR/J014699/1
VIA 013
Keywords: Science & Technology
Life Sciences & Biomedicine
Pharmacology & Pharmacy
Cystic fibrosis
gene therapy
lung
viral vector
non-viral vector
TRANSMEMBRANE CONDUCTANCE REGULATOR
LONG-TERM SAFETY
NASAL POTENTIAL DIFFERENCE
CHLORIDE TRANSPORT DEFECT
AIRWAY EPITHELIAL-CELLS
PLURIPOTENT STEM-CELLS
PHASE 2B TRIAL
RECOMBINANT ADENOVIRUS
LENTIVIRAL VECTOR
CFTR GENE
Publication Status: Published
Appears in Collections:National Heart and Lung Institute